Patients & families
- In this section:
- Patients & families
- The INPDR - your registry
- FAQs
We all want to see people with Niemann-Pick disease living full and positive lives. As a family with experience of the disease, you play such an important role.
By contributing your experience to our Patient Reported Database, you will support clinical research and provide real-world evidence to determine the efficacy of therapeutics. In the process, you’ll be helping us create real, positive change. Sign up.
